Scotland begins testing newborn babies for rare genetic condition

Spinal Muscular Atrophy (SMA) causes progressive muscle weakness and, without treatment, can limit life expectancy to just ...
Medical Xpress

Nervous System Diseases: News and Research on Muscular Atrophy, Spinal

The U.S. Food and Drug Administration has approved Itvisma (onasemnogene abeparvovec-brve) for the treatment of spinal muscular atrophy (SMA) in patients 2 years and older with confirmed mutation in ...
Nasdaq

Biogen Announces Promising Interim Phase 1 Results for Salanersen (BIIB115/ION306) in Treatment of Spinal Muscular Atrophy

Biogen Inc. announced positive interim results from a Phase 1 study of salanersen (BIIB115/ION306), a novel antisense oligonucleotide for treating spinal muscular atrophy (SMA). The data show that ...
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What is SMA? The rare genetic condition that Jesy Nelson’s twins have

Former Little Mix star Jesy Nelson revealed her twin daughters, Ocean Jade and Story Monroe Nelson-Foster, had been diagnosed with Spinal Muscular Atrophy (SMA) Type 1, a rare genetic condition that ...