Musculoskeletal (MSK) disorders affect the muscles, bones, joints, and tissues. In children, they may be due to infection, cancer, inflammatory arthritis, or progressive muscle disorders. MSK ...

Amyotrophic lateral sclerosis (ALS) affects the nerve cells in the brain and spinal cord that control muscle movement. Different types of ALS cause symptoms to begin in a certain part of the body and ...

More than 30 rare muscular dystrophy types cause progressive muscle weakness from inherited gene mutations. Combined, they affect about 1 in 5,000 to 8,000 people. Common subtypes vary by age of onset ...

Early trial data suggest RNA therapies SRP-1001 and SRP-1003 reach muscle and show biomarker activity in muscular dystrophy.